Companies related to orphan diseases

Always Ahead

First-in-kind stem cell therapy to combat neurodegenerative diseases, giving back treatment perspective to millions

DRG Turns Physician-Made Clinical Discoveries Into Accessible Drugs

FOR RARE, BY RARE

Specialty Plasma-Derived Therapeutics

Healing the disease that causes cancer

Alone we are rare. Together we are strong.®

AOP Health is the European pioneer for integrated therapies for rare diseases and in critical care.

Tenacious in our search for transformative therapies

We are a late-stage biopharmaceutical company focused on developing & commercializing products to treat rare diseases

Shifting the treatment paradigm for neurodegenerative disease towards precision medicine and disease prevention.

Supply chain specialist for rare & orphan diseases' medicines in the pharmaceutical industry

aTyr is a biotherapeutics company engaged in the development of innovative medicines based on novel biology.